Organizations advancing AAV-based therapies for serious, rare, and underserved diseases. Access manufacturing expertise and production capacity that supports programs from early research through development.
Research teams working to transform scientific discoveries into therapeutic opportunities. Generate research-grade AAV material for proof-of-concept studies, translational research, and early-stage program development.
Organizations championing the needs of patients and families affected by rare and complex diseases. Accelerate therapeutic development through program development.
Organizations advancing rare and complex disease research through innovative technologies, platforms, and data-driven solutions.